Gene Therapy

Gathering and Disseminating Standardized Gene Therapy Data: The WFH Gene Therapy Registry

Author(s):

Barbara Konkle, Flora Peyvandi, Mayss Naccache, Toong Youttananukorn, Wolfgang Miesbach, Brian O’Mahony, Mike Makris, Tadashi Matsushita, Steven Pipe, Tammuella Chrisentery-Singleton, Mark Skinner, Donna Coffin, Glen Pierce
Publication:
European Association for Haemophilia and Allied Disorders (EAHAD) 17th Annual Congress 2024
Date:
February 6-9, 2024
Topics:
gene therapy, WFH Gene Therapy Registry, registry

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