ATHN 8

Inhibitor development and clinical characteristics in children with severe hemophilia A in the ATHN 8 US Cohort Study

Author(s):

Courtney D. Thornburg, H. Marijke van den Berg, Martin Chandler, Lynn Malec, Matthew Manuel, Carrie O’Neill, Michael Recht, Elizabeth Taggart, Shannon L. Carpenter for the American Thrombosis and Hemostasis Network (ATHN) 8 investigators study group
Publication:
Blood Vessels, Thrombosis & Hemostasis Journal
Date:
June 16, 2025
Topics:
Hemophilia, Inhibitors, Children

Real-World Use of Recombinant Factor IX Fusion Protein in Previously Untreated Patients with Congenital Hemophilia B from the ATHN 8 Study

Author(s):

Courtney Thornburg, Martin Chandler, Lynn Malec, Matthew Manuel, Carrie O’Neill, Michael Recht, Elizabeth Taggart, Hongseok Kim, Vindhi Desai, Hiren Shah, Shannon Carpenter
Publication:
Thrombosis & Hemostasis Summit of North America (THSNA) 2024
Date:
April 4-6, 2024
Topics:
recombinant factor IX, previously untreated patients, PUPs, hemophilia B, ATHN 8

U.S. Cohort Study of Previously Untreated Patients with Congenital Hemophilia (ATHN 8: PUPs Study): Inhibitor Development and Treatment Characteristics

Author(s):

Shannon L Carpenter, Martin Chandler, Michael F Guerrera, Lynn Malec, Matthew Manuel, Michael Recht, Ulrike Reiss, Robert F Sidonio Jr, Cristina Tarango, Marijke Van den Berg, Michael Wang, Courtney D Thornburg
Publication:
Blood
Date:
November 15, 2022
Topics:
Interim Analysis, PUPs

U.S. Cohort Study of Previously Untreated Patients with Congenital Hemophilia (ATHN 8: PUPs Study): Association Between Family History and Age of Diagnosis

Author(s):

Courtney Thornburg, Kenneth Friedman, Michael Guerrera, Chunla He, Lynn M Malec, Mindy L Simpson, Michael D Tarantino, Marijke Van Den Berg, Crystal Watson, Shannon L Carpenter
Publication:
Blood
Date:
November 5, 2020
Topics:
Children, PUPs, Congenital Hemophilia

U.S. Cohort Study of Previously Untreated Patients with Congenital Hemophilia (ATHN 8: PUPs Matter Study): Interim Analysis of the 2010-2019 Birth Cohort

Author(s):

Shannon Carpenter, Chunla He, Lynn Malec, Amanda Payne, Marijke van den Berg, Crystal Watson, Courtney Thornburg
Publication:
International Society on Thrombosis and Haemostasis (ISTH) 2020 Virtual Congress
Date:
July 11-14, 2020
Topics:
Hemophilia, PUPs

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